
Scientists Fix Genetic Defect in Mice Tied to Brain Disorders That Include Autism and Epilepsy
Gene therapy successfully reduced epileptic activity, hyperactivity and risk-taking behaviors tied to SYNGAP1-related disorders SEATTLE, WA, UNITED STATES, October 9, 2025 /EINPresswire.com/ -- In an exciting scientific first, researchers at the Allen Institute successfully designed a new gene therapy that reversed symptoms related to SYNGAP1-related disorders (SRD) in mice. These are a class of brain disorders that can lead to severe and debilitating symptoms including intellectual disability, epilepsy, …